You are using an unsupported browser. Please update your browser to the latest version on or before July 31, 2020.

Showing articles from therapeutic advances tag

Deep Dive – Contextualizing Endpoints and Therapeutic Advances in Rare Disease

**Understanding the Landscape for Rare Disease Endpoints** * New developments/approaches & trends * Regulatory openness to complex and innovative endpoints **Measuring Burden of Illness and Quality of Life: Aligning What’s Meaningful Between Patients & Researchers** * Opportunities to improve identification o…

scroll to top icon