_***Recommended for Young Investigators/Researchers**_ **Strategies for Successful Research in Small Patient Populations** * Discuss how to support and engage in research activities and develop interest for small patient population studies **Understanding Measurement Tools to Capture Patient Data in Rare and Ultr…
_***Recommended for Young Investigators/Researchers**_ **Addressing the Need for Innovative Clinical Trials to Advance Rare Disease Therapies** * Challenges in traditional double-blind randomized clinical trial design for rare disease studies * Ethics and access to clinical trials in rare disease research **Bas…